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Food or medicine? A European regulatory perspective on nutritional therapy products to treat inborn errors of metabolism
Stolwijk, N. N., Bosch, A. M., Bouwhuis, N., Häberle, J., van Karnebeek, C., van Spronsen, F. J., Langeveld, M. & Hollak, C. E. M., Nov 2023, In: Journal of Inherited Metabolic Disease. 46, 6, p. 1017-1028 12 p.Research output: Contribution to journal › Article › Academic › peer-review
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Development of medicines for rare diseases and inborn errors of metabolism: Toward novel public–private partnerships
Rosenberg, N., Stolwijk, N. N., van den Berg, S., Heus, J. J., van der Wel, V., van Gelder, T., Bosch, A. M., de Visser, S. J. & Hollak, C. E. M., Sept 2023, In: Journal of Inherited Metabolic Disease. 46, 5, p. 806-816 11 p.Research output: Contribution to journal › Review article › Academic › peer-review
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Access to medicines for rare diseases: A European regulatory roadmap for academia
Rosenberg, N., van den Berg, S., Stolwijk, N. N., Jacobs, B. A. W., Post, H. C., Pasmooij, A. M. G., de Visser, S. J. & Hollak, C. E. M., 2023, In: Frontiers in Pharmacology. 14, 1142351.Research output: Contribution to journal › Article › Academic › peer-review
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