-
Human post-mortem organotypic brain slice cultures: a tool to study pathomechanisms and test therapies
Plug, B. C., Revers, I. M., Breur, M., González, G. M., Timmerman, J. A., Meijns, N. R. C., Hamberg, D., Wagendorp, J., Nutma, E., Wolf, N. I., Luchicchi, A., Mansvelder, H. D., van Til, N. P., van der Knaap, M. S. & Bugiani, M., Dec 2024, In: Acta Neuropathologica Communications. 12, 1, p. 1-17 17 p., 83.Research output: Contribution to journal › Article › Academic › peer-review
-
In vivo base editing of a pathogenic Eif2b5 variant improves vanishing white matter phenotypes in mice
Böck, D., Revers, I. M., Bomhof, A. S. J., Hillen, A. E. J., Boeijink, C., Kissling, L., Egli, S., Moreno-Mateos, M. A., van der Knaap, M. S., van Til, N. P. & Schwank, G., 1 May 2024, In: Molecular therapy. 32, 5, p. 1328-1343 16 p.Research output: Contribution to journal › Article › Academic › peer-review