Amsterdam Reproduction & Development
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Controlled access to lumasiran in primary hyperoxaluria type 1: evaluation of a new access route for orphan drugs in the Netherlands
Deesker, L. J., Franssen, C. F. M., Dorresteijn, E., van de Kar, N. C. A. J., Nurmohamed, S. A., Severs, D., Garrelfs, S. F., Pisters-van Roy, A. A. M. G., Hollak, C. E. M. & Groothoff, J. W., 1 Oct 2025, In: Nephrology, dialysis, transplantation : official publication of the European Dialysis and Transplant Association - European Renal Association. 40, 10, p. 1887-1896 10 p.Research output: Contribution to journal › Article › Academic › peer-review
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Global access to management of primary hyperoxaluria: A survey on behalf of OxalEurope, G&K Working Group of the ERA and ESPN
Deesker, L. J., Oubram, L., Almardini, R., Baum, M. A., Bonilla-Felix, M., Figueres, L., Garrelfs, S. F., Groothoff, J. W., Ekulu, P. P. M., Müller, R.-U., Oosterveld, M. J. S., Qian, S., Sayer, J. A., Soliman, N., Moochhala, S. H. & Bacchetta, J., 1 Sept 2025, In: Nephrology dialysis transplantation. 40, 9, p. 1688-1697 10 p.Research output: Contribution to journal › Article › Academic › peer-review
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New opportunities for accessing promising non-oncological orphan drugs
Hollak, C. E. M., Reparon-Schuijt, C. C., Verdeyen, K., Deesker, L. J., Groothoff, J. W., Vos, J. M. I., Huisman, A. H., van der Flier, S. & Pisters-van Roy, A. A. M. G., 1 May 2025, In: The Lancet Regional Health - Europe. 52, p. 101275 101275.Research output: Contribution to journal › Comment/Letter to the editor › Academic
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