-
Medicine Development and Access for Rare Diseases: Can We Do Better?
Hollak, C. E. M., Rosenberg, N., Post, C., Stolwijk, N., Manders, E., Schoenmakers, D., Penninx, B., Reijnhout, N., Verdeyen, K., Jonker, R., Bosch, A. M., Langeveld, M., van der Wel, V., de Visser, S. & van den Berg, S., Mar 2026, In: Journal of inherited metabolic disease. 49, 2, p. e70146 e70146.Research output: Contribution to Journal › Review article › Academic › peer-review
-
Navigating the regulatory labyrinth to promote patient access to medicine for rare diseases
Rosenberg, N., 2026, 278 p.Research output: PhD Thesis › PhD-Thesis - Research and graduation internal
-
Access to anticancer and orphan medicines through compassionate use programs and named patient basis in seven European countries
Rosenberg, N., Post, H. C., Schutte, T., de Visser, S. J., Bartelink, I., Pasmooij, A. M. G., van Laarhoven, H. W. M. & Hollak, C. E. M., 1 Nov 2025, In: ESMO open. 10, 11, 105855.Research output: Contribution to Journal › Article › Academic › peer-review
- All publications
